Pharmacology/Part 9/9.6 Bone Metabolism

9.6 Bone Metabolism Drugs

Bone metabolism pharmacology targets osteoporosis, Paget's disease, and hypercalcemia through agents that modulate osteoclast and osteoblast activity.

Bisphosphonates

Mechanism & Clinical Use

Pyrophosphate analogs that bind hydroxyapatite in bone. Inhibit osteoclast activity (induce apoptosis, inhibit farnesyl pyrophosphate synthase). Decrease bone resorption.

Agents:

  • Alendronate: Oral daily/weekly; osteoporosis
  • Risedronate: Oral; osteoporosis, Paget's disease
  • Ibandronate: Oral monthly or IV quarterly
  • Zoledronic acid: IV yearly; most potent; hypercalcemia of malignancy

Administration (Oral):

  • • Take on empty stomach with water
  • • Remain upright 30-60 min (prevent esophagitis)
  • • No food/drink for 30 min

Adverse Effects:

  • • Esophagitis, GI upset (oral forms)
  • • Osteonecrosis of jaw (rare; dental procedures)
  • • Atypical femoral fractures (long-term use)
  • • Hypocalcemia, flu-like symptoms (IV)

RANKL Inhibitor

Denosumab

Monoclonal antibody against RANKL (receptor activator of NF-κB ligand). Prevents RANK-RANKL interaction, inhibiting osteoclast formation/activation. More potent than bisphosphonates.

Indications:

  • • Osteoporosis (subcutaneous every 6 months)
  • • Bone metastases, giant cell tumor
  • • Alternative if bisphosphonates not tolerated

Adverse Effects:

  • • Hypocalcemia (give Ca²⁺ and vitamin D supplements)
  • • Osteonecrosis of jaw
  • • Atypical femoral fractures
  • • Serious infections (skin, GI, urinary)
  • ⚠️ Rapid bone loss if discontinued (rebound effect)

Anabolic Agents

Teriparatide

Recombinant PTH (1-34 fragment). Intermittent dosing stimulates osteoblasts → bone formation. (Note: Continuous PTH causes bone resorption via RANKL.)

  • • Severe osteoporosis, high fracture risk
  • • Daily subcutaneous injection (up to 2 years)
  • ⚠️ Osteosarcoma (animal studies); contraindicated in Paget's, prior radiation

Abaloparatide

PTH-related peptide analog. Similar to teriparatide but more selective for anabolic pathways.

  • • Postmenopausal osteoporosis
  • • Daily subcutaneous (up to 18 months)
  • • Similar warnings to teriparatide

Romosozumab

Monoclonal antibody against sclerostin (SOST protein). Dual effect: ↑ bone formation (↑ osteoblasts), ↓ bone resorption (↓ osteoclasts).

  • • Postmenopausal osteoporosis, high fracture risk
  • • Monthly subcutaneous for 12 months
  • ⚠️ Cardiovascular risk (MI, stroke); contraindicated in recent MI/stroke

Calcium & Vitamin D

Calcium Supplements

  • Calcium carbonate: 40% elemental Ca; take with food (needs acid)
  • Calcium citrate: 21% elemental Ca; better absorption; can take without food
  • • Adjunct to all osteoporosis therapies
  • Target 1000-1200 mg/day; adverse: constipation, kidney stones

Vitamin D

  • Cholecalciferol (D3): Supplementation, deficiency
  • Ergocalciferol (D2): Alternative form
  • Calcitriol (1,25-(OH)₂D₃): Active form; hypoparathyroidism, CKD
  • • Essential for calcium absorption
  • Target 800-1000 IU/day; toxicity: hypercalcemia, kidney stones

Calcitonin

Hormone from thyroid C-cells. Inhibits osteoclast activity, ↓ bone resorption, ↓ serum calcium. Less effective than bisphosphonates.

Indications:

  • • Paget's disease (salmon calcitonin)
  • • Hypercalcemia (acute management)
  • • Osteoporosis (nasal spray; less used now)

Adverse Effects:

  • • Nausea, flushing (salmon calcitonin)
  • • Nasal irritation (intranasal)
  • • Possible cancer risk (long-term)
  • • Tachyphylaxis (decreased response over time)