Pharmacology/Part 9/9.1 Hypothalamic-Pituitary

9.1 Hypothalamic-Pituitary Drugs

The hypothalamic-pituitary axis regulates multiple endocrine systems through releasing hormones and pituitary hormones. Pharmacological interventions target hormone deficiencies, excesses, and reproductive disorders.

Hypothalamic-Pituitary Axis

Hypothalamus → Releasing/Inhibiting hormones → Anterior pituitary → Tropic hormones → Target organs

GnRH Analogs

Mechanism & Clinical Applications

GnRH Agonists: Continuous administration desensitizes GnRH receptors, paradoxically suppressing LH/FSH (after initial surge). Used for hormone-sensitive cancers and precocious puberty.

Agonists:

  • Leuprolide, goserelin: Prostate cancer, endometriosis, uterine fibroids
  • • Initial flare (add antiandrogen for prostate cancer)
  • Adverse: Hot flashes, bone loss, impotence

GnRH Antagonists: Immediate suppression of LH/FSH without initial surge.

Antagonists:

  • Degarelix, elagolix: Prostate cancer, endometriosis
  • • No tumor flare
  • • Faster suppression than agonists

Growth Hormone (GH)

Somatropin (Recombinant GH)

Indications:

  • • GH deficiency in children (↑ growth velocity)
  • • Turner syndrome, Prader-Willi syndrome
  • • Chronic kidney disease
  • • AIDS-related wasting

Adverse Effects:

  • • Hyperglycemia, insulin resistance
  • • Peripheral edema
  • • Arthralgias, carpal tunnel syndrome
  • • Increased ICP (pseudotumor cerebri)
  • • Slipped capital femoral epiphysis

GH Antagonists

Octreotide, Lanreotide

  • • Somatostatin analogs (long-acting)
  • Use: Acromegaly, carcinoid tumors, VIPomas
  • • ↓ GH, ↓ IGF-1, ↓ tumor hormone secretion
  • Adverse: GI upset, gallstones, glucose intolerance

Pegvisomant

  • • GH receptor antagonist
  • Use: Acromegaly (refractory to somatostatin analogs)
  • • Blocks GH effects (↓ IGF-1)
  • Adverse: Hepatotoxicity (monitor LFTs)

ADH (Vasopressin) & Analogs

Desmopressin (DDAVP)

Mechanism:

Selective V2 receptor agonist. Increases water reabsorption in collecting duct via aquaporin-2 insertion. Minimal V1 activity (no vasoconstriction).

Indications:

  • Central diabetes insipidus
  • • Nocturnal enuresis (bedwetting)
  • • Hemophilia A, von Willebrand disease (↑ vWF, factor VIII)

⚠️ Major Risk:

Hyponatremia: Water retention without electrolyte reabsorption. Monitor sodium levels, especially in elderly.

Restrict fluid intake to prevent water intoxication

ADH Antagonists (Vaptans)

Conivaptan, Tolvaptan

  • • V2 receptor antagonists ("aquaretics")
  • Use: SIADH, hyponatremia (euvolemic/hypervolemic)
  • • ↑ Free water excretion without electrolyte loss
  • ⚠️ Correct Na+ slowly (avoid osmotic demyelination syndrome)

Clinical Notes

  • • Do NOT use in hypovolemic hyponatremia (give NS)
  • Adverse: Hypernatremia, thirst, polyuria
  • • Hepatotoxicity (tolvaptan); restrict duration

Oxytocin & Analogs

Clinical Applications in Obstetrics

Oxytocin:

  • Labor induction: Stimulates uterine contractions (↑ PGF2α, ↑ Ca²⁺)
  • Postpartum hemorrhage: Prevents/treats uterine atony
  • • IV infusion (titrate to effect)
  • • Also involved in milk letdown reflex

Adverse Effects:

  • Uterine hyperstimulation: Fetal distress, uterine rupture
  • • Water intoxication (ADH-like effects at high doses)
  • • Hypotension (rapid IV bolus)

Contraindications:

  • • Cephalopelvic disproportion
  • • Abnormal fetal position
  • • Placenta previa/abruptio

Prolactin Modulators

Dopamine Agonists

Dopamine tonically inhibits prolactin release via D2 receptors. Agonists suppress prolactin, shrink prolactinomas.

  • Bromocriptine:
    • • Ergot derivative; D2 agonist
    • • Hyperprolactinemia, prolactinomas
    • • Adverse: Nausea, orthostatic hypotension, hallucinations
  • Cabergoline:
    • • Longer half-life, better tolerated
    • • Weekly dosing
    • • Preferred over bromocriptine

Clinical Scenarios

Hyperprolactinemia

  • • Galactorrhea, amenorrhea, infertility
  • • Hypogonadism (prolactin ↓ GnRH)
  • • First-line: Dopamine agonists

Prolactinomas

  • • Most common pituitary tumor
  • • Medical therapy (cabergoline) shrinks tumors
  • • Surgery if refractory or compressive symptoms